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FDA panel unanimously endorses Spark's gene therapy for rare blindness pioneered at CHOP

Philly.com / Business 49 sources

Gene therapy developed at Children's Hospital of Philadelphia gets a unanimous endorsement from FDA advisers to treat rare inherited blindness.

FDA Panel Endorses Gene Therapy For A Form Of Childhood Blindness

NPR

Food and Drug Administration advisers unanimously recommended that the agency approve the first gene therapy for an inherited disease — a rare defect that causes blindness in children.

Why FDA's approval of a gene therapy to treat form of blindness is a big deal

CBS News / Health

An FDA advisory panel gave the green light for a therapy that can improve the vision of people with a rare genetic disorder called Leber's congenital amaurosis (LCA)

FDA advisers urge approval for first gene therapy for inherited disease

The treatment targets a rare form of childhood blindness caused by a defective gene.

FDA reviews gene therapy to treat form of blindness

CBS News / Health

If approved, it would be the first gene therapy in the U.S. for an inherited disease

Spark Therapeutics jumps after favorable FDA panel vote

CNBC / U.S.

CNBC's Meg Tirrell reports on Spark Therapeutics shares jumping after the FDA panel votes in favor of the company's gene therapy.

FDA Vote Sets Stage for Gene Therapy’s Future

The pioneering treatment fixes a mutated gene and could soon be available in the U.S.

The Latest: FDA advisers endorse gene therapy for blindness

SILVER SPRING, Md. (AP) — The Latest on an FDA panel's discussion on a gene therapy treatment for blindness (all times local):; 3:19 p.m. U.S. health advisers have endorsed an experimental approach to treating inherited blindness, setting…

FDA advisers endorse gene therapy to treat form of blindness

SILVER SPRING, Md. (AP) — A potentially groundbreaking treatment for a rare form of blindness moved one step closer to U.S. approval Thursday, as federal health advisers endorsed the experimental gene therapy for patients with an inherited…

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